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GEMMABio
Company
Team
Board of Directors
Investors
Partners
SMA1
Expanded Access Policy
News
Press Releases
Publications
Presentations
Commentary
Careers
Contact
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Press Releases


November 24, 2025

GEMMABio Announces Clinical Trial Authorization for New SMA1 Gene Therapy

October 7, 2025

GEMMABio Launches Rare Therapeutics, Inc. to Develop and Deliver Gene Therapies for Ultra‑Orphan Diseases

January 9, 2025

Gene Therapy Pioneer Jim Wilson Comments on iECURE's Announcement of Complete Clinical Response for ECUR-506

January 8, 2025

Gene Therapy Pioneer Jim Wilson Comments on Solid Biosciences's Announcement of FDA IND Clearance for Friedreich's Ataxia Treatment

GEMMABio Appoints Dr. May Orfali as Chief Medical Officer

December 23, 2024

GEMMABio Secures $34 Million in Seed Funding to Drive Gene Therapy Advancements

October 8, 2024

GEMMABio Announces $100 Million Agreement with Brazil's Leading Health Research Institute

July 31, 2024

To Further Advance Gene Therapy Research, Industry Pioneer Jim Wilson is Forming Two Independent Companies Dedicated to Genetic Medicine

GEMMA Biotherapeutics

125 S. 31st St.
Philadelphia, PA 19104

(445) 201-3569
info@gemmabiotx.com

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